Posts
Sawyer’s CHAMP1 Story
Learn more about Sawyer’s CHAMP1 story.
Read MoreKate’s Memorable Story
Learn more about Kate’s rare disease story.
Read MoreEvan’s MED13L Story
Hear about Evan’s experience with his new MED13L diagnosis.
Read MoreFamily Stories // Historias Familiares: Gabriel (CTNNB1)
Simons Searchlight shares the story of Gabriel and his family’s journey.
Read MoreTommy’s Rare Disease Story
Karen shares her family’s rare disease journey.
Read MoreSimons Searchlight Member Amber Freed Looks for a Gene Therapy “Miracle”
Learn more about Amber Freed’s quest to find answers.
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